Challenges For People With MPS1
As one of over 6,000 rare diseases, money for MPS1 research is scarce and therefore promising new treatments are often delayed. While there is currently no cure for MPS1, the success of bone marrow transplants and enzyme replacement therapy have given people with MPS1 the chance to lead a longer life.
However, because it is degenerative, those with MPS1 endure multiple surgical procedures, pain and disfigurement as the disease progresses, and a shortened life span.
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Inspiring Others To Fight MPS1
Through the generous donations raised by Erik's Chance fundraising events, the MPS1 Research Foundation presented a check in the amount of $60,000 to the Icahn School of Medicine at Mount Sinai to support an important new research project using Pentosan Polysulfate (PPS) as a new treatment approach for the skeletal disease in MPS 1.
Erik is now twelve years old. His caring spirit and positive attitude, despite all of the challenges and surgeries he endures, inspired his family to create the MPS1 Research Foundation.
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MPS1: A Deadly Disease
Mucopolysaccharidosis 1 (MPS1) is a genetic lysosomal storage disease caused by the body’s inability to produce the enzyme, alpha-L-iduronidase.
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How You Can Help
There are many different ways you can support the hard work of scientists and doctors helping ease the pain and suffering of those with this terrible disease.
Learn How To Help Those With MPS1